Therapeutic areas of concentration
Lambert-Eaton Myasthenic Syndrome (LEMS)
For more information about the 1st LEMS trial, click here or go to clinicaltrials.gov.
For more information about the 2nd LEMS trial, click here or go to clinicaltrials.gov.
Muscle-Specific Receptor Tyrosine Kinase Myasthenia Gravis (MuSK-MG)
In 2018, Catalyst is recruiting patients for a phase 3 trial to evaluate the efficacy and safety of amifampridine phosphate in the treatment of MuSK-MG. The primary efficacy endpoint of THE MuSK Trial will be the degree to which amifampridine phosphate may help improve the daily activities in patients with MuSK-MG, as measured by improvement in MG-ADL score compared with placebo. The FDA has assigned amifampridine phosphate an orphan drug designation in MuSK-MG. For more information about the trial itself go to clinicaltrials.gov.
MG-ADL=myasthenia gravis activities of daily living.