Catalyst pharmaceuticals—working toward a brighter future for everyone affected by a rare disease

Organizations dedicated to helping people with rare diseases

Catalyst Pharmaceuticals partners with advocacy organizations to support patients and the rare disease community. The following organizations can provide information and assistance in dealing with neuromuscular and other rare diseases.

Child Neurology Foundation (CNF)

Established in 2001, the Child Neurology Foundation serves pediatric patients through advocacy, education, research, and support initiatives. Its mission is to serve as a collaborative center of education and support for caregivers and their children with neurologic conditions. Learn More

Global Genes

Global Genes is a leading rare disease advocacy organization with global reach to the worldwide rare community of patients, caregivers, advocates, and clinical partners. Its mission is to eliminate the challenges of rare disease. Learn More

Living with LEMS

Part of the Global Genes community, is a site for all patients with Lambert-Eaton myasthenic syndrome (LEMS) and their caregivers and family members that offers information, resources, and support. The goals of this site are to build connections and offer resources and support to help LEMS patients become informed advocates. Learn More

National Organization for Rare Disorders (NORD)

Established in the late 1970s and early 1980s, NORD is a patient advocacy organization dedicated to individuals with rare diseases and the organizations that serve them.  NORD, along with its more than 260 patient organization members, is committed to the identification, treatment, and cure of rare disorders through programs of education, advocacy, research, and patient services. Learn More

Muscular Dystrophy Association (MDA)

Established in June 1950, the Muscular Dystrophy Association is committed to saving and improving the lives of kids and adults living with muscular dystrophy, amyotrophic lateral sclerosis (ALS), and related muscle-debilitating diseases that take away physical strength, independence, and life. Learn More

Myasthenia Gravis Foundation of America (MGFA)

The Myasthenia Gravis Foundation of America is the only national volunteer health agency in the United States dedicated solely to the fight against myasthenia gravis. MGFA is committed to finding a cure for myasthenia gravis and closely related disorders, improving treatment options, and providing information and support to people with myasthenia gravis, through research, education, community programs, and advocacy. Learn More

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